New Gene Delivery Systems Target Brain Cells | JQJO

NIH-funded researchers have developed advanced gene delivery systems for precise targeting of brain and spinal cord cells. These systems, using modified adeno-associated viruses (AAVs), enable targeted gene therapy for various neurological disorders. The toolkit includes dozens of delivery systems for different cell types and AI-powered software to identify genetic switches. This breakthrough allows for more accurate research and potential treatments for conditions like ALS, Parkinson's, and Alzheimer's, significantly advancing our understanding of the brain.